504. Restoration of Dystrophin Expression by Gene Editing with S. aureus Cas9 in Models of Duchenne Muscular Dystrophy
Robinson-Hamm, Jacqueline N., Nelson, Christopher E., Rivera, Ruth M. Castellanos, Aartsma-Rus, Annemieke, Asokan, Aravind, Gersbach, Charles A.Volume:
24
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)33313-5
Date:
May, 2016
File:
PDF, 326 KB
english, 2016