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581. Correcting Exon Skipping Splicing Defects in BTK RNA by Using Bifunctional Oligonucleotides
Smith, C.I. Edvard, Bestas, Burcu, Turunen, Janne J., Wengel, JesperVolume:
24
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)33389-5
Date:
May, 2016
File:
PDF, 326 KB
english, 2016