690. Development of a Clinical Lentiviral Vector for Gene Therapy of SCID-X1
Charrier, Sabine, Poletti, Valentina, Martin, Samia, Gjata, Bernard, Hebben, Matthias, Vignaud, Alban, Zhang, Fang, Buckland, Karen, Rothe, Michael, Schambach, Axel, Gaspar, Bobby, Thrasher, Adrian, MVolume:
24
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)33498-0
Date:
May, 2016
File:
PDF, 315 KB
english, 2016