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738. Engineered MicroRNA Silences C9ORF72 Variants in BAC Transgenic Mouse
Cabrera, Gabriela Toro, Peters, Owen M., Gendron, Tania F., Gruntman, Alisha, Brown, Robert H., Mueller, ChristianVolume:
24
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)33546-8
Date:
May, 2016
File:
PDF, 298 KB
english, 2016