741. Development of LNA Gapmer Oligonucleotide Based Therapy for FTD/ALS Caused by the C9orf72 Repeat Expansion
Aoki, Yoshitsugu, Manzano, Raquel, Takeda, Shin'ichi, Talbot, Kevin, Wood, MatthewVolume:
24
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)33549-3
Date:
May, 2016
File:
PDF, 298 KB
english, 2016