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759. Reduction of HLH-like Manifestations in Murine Model of Munc13-4 Deficiency Following Lentiviral Gene Transfer into Hematopoietic Stem and Progenitor Cells
Soheili, Tayebeh-Shabi, Sepulveda, Fernando, Durand, Amandine, Rivière, Julie, Martin, Samia, de Saint Basile, Geneviève, Cavazzana, Marina, André-Schmutz, IsabelleVolume:
24
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)33567-5
Date:
May, 2016
File:
PDF, 299 KB
english, 2016