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183. Developing Strategies To Improve the Current Clinical Vector AAV1-CB-AAT for Alpha-One Antitrypsin Deficiency
Borel, Florie, Choudhury, Sourav, Aslanidi, George, Song, Lina, Kocabas, Evren, Sun, Huaming, Tang, Qiushi, Srivastava, Arun, Wagner, Kathryn, Esteves, Miguel, Flotte, Terence, Mueller, ChristianVolume:
23
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)33788-1
Date:
May, 2015
File:
PDF, 245 KB
english, 2015