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279. Efficient and Safe Lentiviral Vector-Mediated Hematopoietic Stem Cell Gene Therapy in MNGIE Mice
Yadak, Rana, Torronteras, Javier T., Pérez, Raquel C., Bogaerts, Elly, de Ruijter, George, Barquinero, Jordi, Marti, Ramon, Smeets, Bert J., Huston, Marshall W., van Til, Niek P., Wagemaker, Gerard, dVolume:
23
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)33888-6
Date:
May, 2015
File:
PDF, 285 KB
english, 2015