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371. AAV-Based Gene Therapy in a Mouse Model of Smith Lemli Opitz Syndrome (SLOS)
Pasta, Saloni Y., Ting, Flora, Tabron, Dorothy, Sun, Sean, Kadakia, Saurin, Shackleton, Cedric, Watson, GordonVolume:
23
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)33980-6
Date:
May, 2015
File:
PDF, 274 KB
english, 2015