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478. Highly Efficient Targeted Gene Addition in CD34+ Hematopoietic Stem/Progenitor Cells by Combining ZFN mRNA and AAV6 Donor Delivery
Wang, Jianbin, Exline, Colin M., DeClercq, Josh, Li, Patrick, Gregory, Philip D., Cannon, Paula M., Holmes, Michael C.Volume:
23
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)34087-4
Date:
May, 2015
File:
PDF, 276 KB
english, 2015