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695. Splice-Correction of X-Linked Agammaglobulinemia in a Human BAC-Transgenic Mouse Model Using Oligonucleotides
Bestas, Burcu, Moreno, Pedro M.D., Blomberg, Emelie K.M., Mohammad, Dara K., Lundin, Karin E., Månsson, Robert, Berglöf, Anna, Wengel, Jesper, Smith, Edvard C.I.Volume:
23
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)34304-0
Date:
May, 2015
File:
PDF, 272 KB
english, 2015