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37. Towards Clinical Translation of Hematopoietic Stem Cell Gene Editing for the Correction of SCID-X1 Mutations
Genovese, Pietro, Schiroli, Giulia, Conway, Anthony, Ferrari, Samuele, Guschin, Dmitry Y., Di Tomaso, Tiziano, Albano, Luisa, Marin, Virna, Giuliani, Erica, Gregory, Philip D., Holmes, Michael C., GenVolume:
24
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)32846-5
Date:
May, 2016
File:
PDF, 351 KB
english, 2016