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93. Development of AAVidua Vector for the Treatment of Cornea Associated Vision Loss in Bone Marrow Treated-Hurler Patients
Vance, Melisa, Llanga, Llanga, Kurtzberg, Joanne, Samulski, Richard Jude, Hirsch, MatthewVolume:
24
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)32902-1
Date:
May, 2016
File:
PDF, 923 KB
english, 2016