321. Deletion of Mutated GAA Repeats from the Intron 1 of...

Molecular Therapy 2016 / 05 Vol. 24

321. Deletion of Mutated GAA Repeats from the Intron 1 of the Frataxin Gene Using the CRISPR System Restores the Protein Expression in a Friedreich Ataxia Model

Ouellet, Dominique L., Rousseau, Joel, Cherif, Khadija, Gérard, Catherine, Gilbert, Renald, Garnier, Alain, Gaillet, Bruno, Beauséjour, Christian, Tremblay, Jacques P.
How much do you like this book?
What’s the quality of the file?
Download the book for quality assessment
What’s the quality of the downloaded files?
Volume:
24
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)33130-6
Date:
May, 2016
File:
PDF, 299 KB
english, 2016
Conversion to is in progress
Conversion to is failed