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733. Somatically Repairing Compound Heterozygous Recessive Mutations by Chromosomal Cut-and-Paste for In Vivo Gene Therapy
Wang, Dan, Mou, Haiwei, Tran, Karen, Li, Jia, Wang, Blake Y., Gessler, Dominic J., Tai, Phillip WL, Su, Qin, Xue, Wen, Gao, GuangpingVolume:
24
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)33541-9
Date:
May, 2016
File:
PDF, 776 KB
english, 2016