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350. Toward Genosafe Endonuclease-Boosted Gene Targeting Using Breakthrough CRISPR/Cas9 for Next Generation Stem Cell Gene Therapy Culminating in Efficient Ex Vivo/In Vivo Gene Repair/Genomic Editing
Bertolotti, RogerVolume:
23
Language:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)33959-4
Date:
May, 2015
File:
PDF, 272 KB
english, 2015