Intrathecal enzyme replacement therapy reverses cognitive decline in mucopolysaccharidosis type I
Nestrasil, Igor, Shapiro, Elsa, Svatkova, Alena, Dickson, Patricia, Chen, Agnes, Wakumoto, Amy, Ahmed, Alia, Stehel, Edward, McNeil, Sarah, Gravance, Curtis, Maher, ElizabethVolume:
173
Language:
english
Journal:
American Journal of Medical Genetics Part A
DOI:
10.1002/ajmg.a.38073
Date:
March, 2017
File:
PDF, 79 KB
english, 2017