Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction
Han, Sang-oh, Ronzitti, Giuseppe, Arnson, Benjamin, Leborgne, Christian, Li, Songtao, Mingozzi, Federico, Koeberl, DwightVolume:
4
Language:
english
Journal:
Molecular Therapy - Methods & Clinical Development
DOI:
10.1016/j.omtm.2016.12.010
Date:
March, 2017
File:
PDF, 1.31 MB
english, 2017