Targeting CPS1 in the treatment of Carbamoyl phosphate synthetase 1 (CPS1) deficiency, a urea cycle disorder
Diez-Fernandez, Carmen, Häberle, JohannesVolume:
21
Language:
english
Journal:
Expert Opinion on Therapeutic Targets
DOI:
10.1080/14728222.2017.1294685
Date:
April, 2017
File:
PDF, 1.22 MB
english, 2017