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RNA Trans-Splicing Targeting Endogenous β-Globin Pre-Messenger RNA in Human Erythroid Cells
Uchida, Naoya, Washington, Kareem N., Mozer, Brian, Platner, Charlotte, Ballantine, Josiah, Skala, Luke P., Raines, Lydia, Shvygin, Anna, Hsieh, Matthew M., Mitchell, Lloyd G., Tisdale, John F.Volume:
28
Language:
english
Journal:
Human Gene Therapy Methods
DOI:
10.1089/hgtb.2016.077
Date:
April, 2017
File:
PDF, 473 KB
english, 2017