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Messenger RNA (mRNA) delivery to the liver corrects ornithine transcarbamylase deficiency in a mouse disease model
Brandt, Gordon, Prieve, Mary, Bell, Eric, Blevins, Teri, Galperin, Anna, Harvie, Pierrot, Li, Allen, Menye, Jean-Rene Ella, Monahan, Sean, Paschal, Amber, Roy, Debashish, Waldheim, Matt, Houston, MichVolume:
120
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2016.11.050
Date:
January, 2017
File:
PDF, 49 KB
english, 2017