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Design and rationale of ongoing observational and treatment studies for BMN 250: a novel enzyme replacement therapy for Sanfilippo syndrome type B
Shaywitz, Adam, Maricich, Stephen, Yu, Hua, Kent, SteveVolume:
120
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2016.11.317
Date:
January, 2017
File:
PDF, 46 KB
english, 2017