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Improvement in pulmonary function and serum immunoglobulin G in long-term enzyme replacement therapy with velmanase alfa(human recombinant alpha-mannosidase) in alpha-mannosidosis patients
Borgwardt, Line, Lund, Allan M, De Meirleir, Linda, Amraoui, Yasmina, Andersen, Oluf, Dolhem, Philippe, Campos, Mercedes Gil, Guffon, Nathalie, Héron, Bénédicte, Jameson, Elisabeth, Jones, Simon A, LaVolume:
120
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2016.11.046
Date:
January, 2017
File:
PDF, 49 KB
english, 2017