Burden of Fabry disease in young patients (≤30 years of age) who were initiated on enzyme replacement therapy with agalsidase beta: a Fabry Registry analysis
Hopkin, Robert J., Brand, Eva, Rasmussen, Ulla F., Germain, Dominique P., Guffon, Nathalie, Jovanovic, Ana, Kantola, Ilkka, Karaa, Amel, Lemay, Roberta, Martins, Ana M., Wilcox, William R., Yoo, Han-WVolume:
120
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2016.11.151
Date:
January, 2017
File:
PDF, 67 KB
english, 2017