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Generation of infantile- and late-onset Pompe disease models using CRISPR-Cas9 genome editing
Huang, Jeffrey Y., Wang, Raymond Y.Volume:
120
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2016.11.156
Date:
January, 2017
File:
PDF, 47 KB
english, 2017