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Is joint pain a criteria for ERT indication in adult patients with MPS IVA and VI, even without significant visceral involvement?
Politei, Juan, Durand, Consuelo, Frabasil, Joaquin, Masllorens, Francisca, Schenone, Andrea BVolume:
120
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2016.11.277
Date:
January, 2017
File:
PDF, 64 KB
english, 2017