Comparison of systemic routes of administration for CLN3 delivery via scAAV9
Kaye Spratt, S., Aldrich, Amy, Padegimas, Linas, Fallet, Rachel W, David, Adam, Miller, Tim, Kielian, Tammy L.Volume:
120
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2016.11.332
Date:
January, 2017
File:
PDF, 44 KB
english, 2017