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Antisense oligonucleotide therapy for spinocerebellar ataxia type 2
Scoles, Daniel R., Meera, Pratap, Schneider, Matthew D., Paul, Sharan, Dansithong, Warunee, Figueroa, Karla P., Hung, Gene, Rigo, Frank, Bennett, C. Frank, Otis, Thomas S., Pulst, Stefan M.Volume:
544
Language:
english
Journal:
Nature
DOI:
10.1038/nature22044
Date:
April, 2017
File:
PDF, 4.62 MB
english, 2017