An AAV9 coding for frataxin clearly improved the symptoms and prolonged the life of Friedreich ataxia mouse models
Gérard, Catherine, Xiao, Xiao, Filali, Mohammed, Coulombe, Zoé, Arsenault, Marie, Couet, Jacques, Li, Juan, Drolet, Marie-Claude, Chapdelaine, Pierre, Chikh, Amina, Tremblay, Jacques PVolume:
1
Year:
2014
Language:
english
Journal:
Molecular Therapy - Methods & Clinical Development
DOI:
10.1038/mtm.2014.44
File:
PDF, 643 KB
english, 2014