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Miglustat therapy in a case of early-infantile Niemann-Pick type C
Usui, Miho, Miyauchi, Akihiko, Nakano, Yuko, Nakamura, Sachie, Jimbo, Eriko, Itamura, Shinji, Adachi, Kaori, Nanba, Eiji, Narita, Aya, Yamagata, Takanori, Osaka, HitoshiLanguage:
english
Journal:
Brain and Development
DOI:
10.1016/j.braindev.2017.05.006
Date:
June, 2017
File:
PDF, 624 KB
english, 2017