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Orkambi® and amplifier co‐therapy improves function from a rare CFTR mutation in gene‐edited cells and patient tissue
Molinski, Steven V, Ahmadi, Saumel, Ip, Wan, Ouyang, Hong, Villella, Adriana, Miller, John P, Lee, Po‐Shun, Kulleperuma, Kethika, Du, Kai, Di Paola, Michelle, Eckford, Paul DW, Laselva, Onofrio, Huan,Language:
english
Journal:
EMBO Molecular Medicine
DOI:
10.15252/emmm.201607137
Date:
June, 2017
File:
PDF, 4.74 MB
english, 2017