Neonatal gene therapy for hemophilia B by a novel adenovirus vector showing sustained transgene expression via a reduction in the leaky expression of viral genes
Iizuka, Shunsuke, Sakurai, Fuminori, Tachibana, Masashi, Ohashi, Kazuo, Mizuguchi, HiroyukiLanguage:
english
Journal:
Molecular Therapy - Methods & Clinical Development
DOI:
10.1016/j.omtm.2017.07.001
Date:
July, 2017
File:
PDF, 1.75 MB
english, 2017