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Safety and efficacy of glycerol phenylbutyrate for management of urea cycle disorders in patients aged 2 months to 2 years
Berry, Susan A., Longo, Nicola, Diaz, George A., McCandless, Shawn E., Smith, Wendy E., Harding, Cary O., Zori, Roberto, Ficicioglu, Can, Lichter-Konecki, Uta, Robinson, Beth, Vockley, JerryLanguage:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2017.09.002
Date:
September, 2017
File:
PDF, 559 KB
english, 2017