Safety and long-term efficacy of AAV4 gene therapy in patients with RPE65 Leber Congenital Amaurosis
Le Meur, Guylène, Lebranchu, Pierre, Billaud, Fanny, Adjali, Oumeya, Schmitt, Sébastien, Bézieau, Stéphane, Péréon, Yann, Valabregue, Romain, Ivan, Catherine, Darmon, Christophe, Moullier, Philippe, RLanguage:
english
Journal:
Molecular Therapy
DOI:
10.1016/j.ymthe.2017.09.014
Date:
September, 2017
File:
PDF, 3.23 MB
english, 2017