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Evaluation of GalNAc-siRNA conjugate activity in pre-clinical animal models with reduced asialoglycoprotein receptor expression
Willoughby, Jennifer L.S., Chan, Amy, Sehgal, Alfica, Butler, James, Nair, Jayaprakash K., Racie, Tim, Shulga-Morskaya, Svetlana, Nguyen, Tuyen, Qian, Kun, Yucius, Kristina, Charisse, Klaus, van BerkeLanguage:
english
Journal:
Molecular Therapy
DOI:
10.1016/j.ymthe.2017.08.019
Date:
September, 2017
File:
PDF, 1.94 MB
english, 2017