Ryanodine channel complex stabilizer compound S48168/ARM210 as a disease modifier in dystrophin-deficient mdx mice: proof-of-concept study and independent validation of efficacy
Capogrosso, Roberta Francesca, Mantuano, Paola, Uaesoontrachoon, Kitipong, Cozzoli, Anna, Giustino, Arcangela, Dow, Todd, Srinivassane, Sadish, Filipovic, Marina, Bell, Christina, Vandermeulen, Jack,Language:
english
Journal:
The FASEB Journal
DOI:
10.1096/fj.201700182rrr
Date:
November, 2017
File:
PDF, 3.24 MB
english, 2017