Impact of long-term elosulfase alfa on activities of daily living in patients with Morquio A syndrome in an open-label, multi-center, phase 3 extension study
Hendriksz, Christian J., Parini, Rossella, AlSayed, Moeenaldeen D., Raiman, Julian, Giugliani, Roberto, Mitchell, John J., Burton, Barbara K., Guelbert, Norberto, Stewart, Fiona J., Hughes, DerralynnLanguage:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2017.11.015
Date:
December, 2017
File:
PDF, 653 KB
english, 2017