Reduction in Brain Heparan Sulfate with Systemic Administration of an IgG Trojan Horse-Sulfamindase Fusion Protein in the Mucopolysaccharidosis Type IIIA Mouse
Boado, Ruben J., Lu, Jeff Zhiqiang, Hui, Eric Ka-Wai, Pardridge, William M.Language:
english
Journal:
Molecular Pharmaceutics
DOI:
10.1021/acs.molpharmaceut.7b00958
Date:
December, 2017
File:
PDF, 2.85 MB
english, 2017