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Long-term sustained effect of liver-targeted AAV gene therapy for MNGIE
Torres-Torronteras, Javier, Cabrera-Pérez, Raquel, Vila-Julia, Ferran, Viscomi, Carlo, Cámara, Yolanda, Hirano, Michio, Zeviani, Massimo, Marti, RamonLanguage:
english
Journal:
Human Gene Therapy
DOI:
10.1089/hum.2017.133
Date:
December, 2017
File:
PDF, 722 KB
english, 2017