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Ataluren-driven Restoration of Shwachman-Bodian-Diamond Syndrome Protein Function in Shwachman-Diamond Syndrome Bone Marrow Cells
Bezzerri, Valentino, Bardelli, Donatella, Morini, Jacopo, Vella, Antonio, Cesaro, Simone, Sorio, Claudio, Biondi, Andrea, Danesino, Cesare, Farruggia, Piero, Assael, Baroukh Maurice, D'Amico, GiovannaLanguage:
english
Journal:
American Journal of Hematology
DOI:
10.1002/ajh.25025
Date:
December, 2017
File:
PDF, 1.10 MB
english, 2017