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Rescue of GSDIII phenotype with gene transfer requires liver- and muscle- targeted GDE expression
Vidal, Patrice, Pagliarani, Serena, Colella, Pasqualina, Verdera, Helena Costa, Jauze, Louisa, Gjorgjieva, Monika, Puzzo, Francesco, Marmier, Solenne, Collaud, Fanny, Sola, Marcelo Simon, Charles, SevLanguage:
english
Journal:
Molecular Therapy
DOI:
10.1016/j.ymthe.2017.12.019
Date:
December, 2017
File:
PDF, 3.00 MB
english, 2017