A novel human muscle cell model of Duchenne muscular dystrophy created by CRISPR/Cas9 and evaluation of antisense-mediated exon skipping
Shimo, Takenori, Hosoki, Kana, Nakatsuji, Yusuke, Yokota, Toshifumi, Obika, SatoshiLanguage:
english
Journal:
Journal of Human Genetics
DOI:
10.1038/s10038-017-0400-0
Date:
January, 2018
File:
PDF, 1.37 MB
english, 2018