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Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy
Calbi, Valeria, Fumagalli, Francesca, Consiglieri, Giulia, Penati, Rachele, Acquati, Serena, Redaelli, Daniela, Attanasio, Vanessa, Marcella, Facchini, Cicalese, Maria Pia, Migliavacca, Maddalena, BarLanguage:
english
Journal:
Bone Marrow Transplantation
DOI:
10.1038/s41409-017-0085-1
Date:
January, 2018
File:
PDF, 576 KB
english, 2018