Novel blood-brain barrier delivery system to treat CNS in MPS II: First clinical trial of anti-transferrin receptor antibody fused enzyme therapy
Okuyama, Torayuki, Sakai, Norio, Yamamoto, Tatsuyoshi, Yamaoka, Mariko, Tomio, TeijiVolume:
123
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2017.12.290
Date:
February, 2018
File:
PDF, 49 KB
english, 2018