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Antisense Therapy for a Common Corneal Dystrophy Ameliorates TCF4 Repeat Expansion-Mediated Toxicity
Zarouchlioti, Christina, Sanchez-Pintado, Beatriz, Hafford Tear, Nathaniel J., Klein, Pontus, Liskova, Petra, Dulla, Kalyan, Semo, Ma’ayan, Vugler, Anthony A., Muthusamy, Kirithika, Dudakova, Lubica,Language:
english
Journal:
The American Journal of Human Genetics
DOI:
10.1016/j.ajhg.2018.02.010
Date:
March, 2018
File:
PDF, 1.82 MB
english, 2018