Efficacy of systemic messenger RNA therapy to treat and prevent porphyria attacks in animal models of acute intermittent porphyria
Jiang, Lei, Berraondo, Pedro, Guey, Lin, Sampedro, Ana, Frassetto, Andrea, Benenato, Kerry, Kalariya, Mayur, Sabnis, Staci, Salerno, Timothy, Kumarasinghe, Ellalahewage, Butcher, William, Lukacs, ChriVolume:
123
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2017.12.175
Date:
February, 2018
File:
PDF, 75 KB
english, 2018