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Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia
Thompson, Alexis A., Walters, Mark C., Kwiatkowski, Janet, Rasko, John E.J., Ribeil, Jean-Antoine, Hongeng, Suradej, Magrin, Elisa, Schiller, Gary J., Payen, Emmanuel, Semeraro, Michaela, Moshous, DesVolume:
378
Language:
english
Journal:
New England Journal of Medicine
DOI:
10.1056/NEJMoa1705342
Date:
April, 2018
File:
PDF, 686 KB
english, 2018