Study of Intraventricular Cerliponase Alfa for CLN2 Disease
Schulz, Angela, Ajayi, Temitayo, Specchio, Nicola, de Los Reyes, Emily, Gissen, Paul, Ballon, Douglas, Dyke, Jonathan P., Cahan, Heather, Slasor, Peter, Jacoby, David, Kohlschütter, AlfriedLanguage:
english
Journal:
New England Journal of Medicine
DOI:
10.1056/NEJMoa1712649
Date:
April, 2018
File:
PDF, 353 KB
english, 2018