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Long term clinical history of an Italian cohort of infantile onset Pompe disease treated with enzyme replacement therapy
Parini, Rossella, De Lorenzo, Paola, Dardis, Andrea, Burlina, Alberto, Cassio, Alessandra, Cavarzere, Paolo, Concolino, Daniela, Della Casa, Roberto, Deodato, Federica, Donati, Maria Alice, Fiumara, AVolume:
13
Language:
english
Journal:
Orphanet Journal of Rare Diseases
DOI:
10.1186/s13023-018-0771-0
Date:
December, 2018
File:
PDF, 699 KB
english, 2018