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Transcriptome analysis in muscle biopsies of late-onset Pompe patients treated with alglucosidase alfa or neoGAA
Zhang, Mindy, Chang, Yi-Chien, Han, Mei, Palmer, Rachel, Baek, Rena, Madden, Stephen, Klinger, KatherineVolume:
123
Language:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2017.12.424
Date:
February, 2018
File:
PDF, 55 KB
english, 2018